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Improved helper virus-free packaging system for HSV amplicon vectors usingan ICP27-deleted, oversized HSV-1 DNA in a bacterial artificial chromosome
MOLECULAR THERAPY
Potential of gene therapy for brain tumors
HUMAN MOLECULAR GENETICS
The importance of gene dosage studies: mutational analysis of the parkin gene in early-onset parkinsonism
HUMAN MOLECULAR GENETICS
Isolation, characterization, and recovery of small peptide phage display epitopes selected against viable malignant glioma cells
CANCER GENE THERAPY
TorsinA: Movement at many levels
NEURON
Neural stem cells display extensive tropism for pathology in adult brain: Evidence from intracranial gliomas (vol 97, pg 12846, 2000)
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
FGF-2 regulation of neurogenesis in adult hippocampus after brain injury
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
Positron emission tomography-based imaging of transgene expression mediated by replication-conditional, oncolytic herpes simplex virus type 1 mutant vectors in vivo
CANCER RESEARCH
A close association of torsinA and alpha-synuclein in Lewy bodies - A fluorescence resonance energy transfer study
AMERICAN JOURNAL OF PATHOLOGY
HSV-1 amplicon vectors - Simplicity and versatility
MOLECULAR THERAPY
Neural precursor cells for delivery of replication-conditional HSV-1 vectors to intracerebral gliomas
MOLECULAR THERAPY
Hybrid vector designs to control the delivery, fate and expression of transgenes
JOURNAL OF GENE MEDICINE
Prodrug activation enzymes in cancer gene therapy
JOURNAL OF GENE MEDICINE
Gene transfer to the nigrostriatal system by hybrid herpes simplex virus/adeno-associated virus amplicon vectors (vol 10, pg 2481, 1999)
HUMAN GENE THERAPY
Correction of acid beta-galactosidase deficiency in GM(1) gangliosidosis human fibroblasts by retrovirus vector-mediated gene transfer: Higher efficiency of release and cross-correction by the murine enzyme
HUMAN GENE THERAPY
Helper virus-free herpes simplex virus type 1 amplicon vectors for granulocyte-macrophage colony-stimulating factor-enhanced vaccination therapy for experimental glioma
HUMAN GENE THERAPY
Gene therapy in the CNS
GENE THERAPY
Quantitation of HSV mass distribution in a rodent brain tumor model
GENE THERAPY
Mutant torsinA, responsible for early-onset torsion dystonia, forms membrane inclusions in cultured neural cells
HUMAN MOLECULAR GENETICS
Parkin deletions in a family with adult-onset, tremor-dominant parkinsonism: Expanding the phenotype
ANNALS OF NEUROLOGY
Evaluation of the role of the D2 dopamine receptor in myoclonus dystonia
ANNALS OF NEUROLOGY
Herpes simplex virus type 1-based amplicon vector systems
ADVANCES IN VIRUS RESEARCH, VOL 55
The GAG deletion of the DYT1 gene is infrequent in musicians with focal dystonia
NEUROLOGY
The genetics of dystonia
NERVENARZT
Neural stem cells display extensive tropism for pathology in adult brain: Evidence from intracranial gliomas
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
Retrograde axonal transport of herpes simplex virus: Evidence for a singlemechanism and a role for tegument
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
A major locus for myoclonus-dystonia maps to chromosome 7q in eight families
AMERICAN JOURNAL OF HUMAN GENETICS
HSV-1 vectors for gene therapy of experimental CNS tumors
GENE THERAPY OF CANCER: METHODS AND PROTOCOLS
Combined HSV-1 recombinant and amplicon piggyback vectors: Replication-competent and defective forms, and therapeutic efficacy for experimental gliomas
JOURNAL OF GENE MEDICINE
Intraarterial delivery of adenovirus vectors and liposome-DNA complexes toexperimental brain neoplasms
HUMAN GENE THERAPY
Gene transfer to the nigrostriatal system by hybrid herpes simplex virus/adeno-associated virus amplicon vectors
HUMAN GENE THERAPY
Selective delivery of herpes virus vectors to experimental brain tumors using RMP-7
CANCER GENE THERAPY
The TOR1A (DYT1) gene family and its role in early onset torsion dystonia
GENOMICS
Gene transfer into the mammalian inner ear using HSV-1 and vaccinia virus vectors
HEARING RESEARCH
Distribution of the mRNAs encoding torsinA and torsinB in the normal adulthuman brain
ANNALS OF NEUROLOGY
Rapid-onset dystonia-parkinsonism: Linkage to chromosome 19q13
ANNALS OF NEUROLOGY
Genetics of primary dystonia
SEMINARS IN NEUROLOGY
Screen for MAOA mutations in target human groups
AMERICAN JOURNAL OF MEDICAL GENETICS
Genetic analysis of three patients with an 18p- syndrome and dystonia
NEUROLOGY
Association of a missense change in the D2 dopamine receptor with myoclonus dystonia
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
Single-step conversion of cells to retrovirus vector producers with herpessimplex virus-Epstein-Barr virus hybrid amplicons
JOURNAL OF VIROLOGY
Multimodal cancer treatment mediated by a replicating oncolytic virus thatdelivers the oxazaphosphorine/rat cytochrome P4502B1 and ganciclovir/herpes simplex virus thymidine kinase gene therapies
CANCER RESEARCH
Squid axoplasm supports the retrograde axonal transport of Herpes simplex virus
BIOLOGICAL BULLETIN
Search for the PARK3 founder haplotype in a large cohort of patients with Parkinson's disease from Northern Germany
ANNALS OF HUMAN GENETICS
Synergistic anticancer effects of ganciclovir thymidine kinase and 5-fluorocytosine cytosine deaminase gene therapies - Response
JOURNAL OF THE NATIONAL CANCER INSTITUTE
Folylpolyglutamyl synthetase gene transfer and glioma antifolate sensitivity in culture and in vivo
JOURNAL OF THE NATIONAL CANCER INSTITUTE
TARGETING GENE-THERAPY VECTORS TO CNS MALIGNANCIES
Journal of neurovirology
NEW PRODRUG ACTIVATION GENE-THERAPY FOR CANCER USING CYTOCHROME-P450 4B1 AND 2-AMINOANTHRACENE 4-IPOMEANOL/
Human gene therapy
Herpes simplex virus type 1 DNA amplified as bacterial artificial chromosome in Escherichia coli: Rescue of replication-competent virus progeny and packaging of amplicon vectors
HUMAN GENE THERAPY
PREEXISTING HERPES-SIMPLEX VIRUS-1 (HSV-1) IMMUNITY DECREASES, BUT DOES NOT ABOLISH, GENE-TRANSFER TO EXPERIMENTAL BRAIN-TUMORS BY A HSV-1 VECTOR
Gene therapy
DE-NOVO MUTATIONS (GAG DELETION) IN THE DYT1 GENE IN 2 NON-JEWISH PATIENTS WITH EARLY-ONSET DYSTONIA
Human molecular genetics (Print)
LONG-TERM SURVIVAL IN A RODENT BRAIN-TUMOR MODEL BY BRADYKININ-ENHANCED INTRAARTERIAL DELIVERY OF A THERAPEUTIC HERPES-SIMPLEX VIRUS VECTOR
Cancer gene therapy
EXCLUSION OF CHROMOSOME REGIONS 6P12 AND 15Q11, BUT NOT CHROMOSOME REGION 7P11, IN A GERMAN FAMILY WITH AUTOSOMAL-DOMINANT CONGENITAL NYSTAGMUS
Genomics (San Diego, Calif.)
CLINICAL AND GENETIC EVALUATION OF A FAMILY WITH A MIXED DYSTONIA PHENOTYPE FROM SOUTH TYROL
Annals of neurology
EXPRESSION OF THE EARLY-ONSET TORSION DYSTONIA GENE (DYT1) IN HUMAN BRAIN
Annals of neurology
ARE MAO-A DEFICIENCY STATES IN THE GENERAL-POPULATION AND IN PUTATIVEHIGH-RISK POPULATIONS HIGHLY UNCOMMON
Journal of neural transmission. Supplementum
THE USE OF RABBIT CYTOCHROME-P450 4B1 AS NEW PRODRUG ACTIVATOR FOR GENE-THERAPY OF HEPATOCELLULAR-CARCINOMA
Hepatology
MONITORING HSV-1-TK AND LACZ GENE DELIVERY AND COEXPRESSION BY A REPLICATION-CONDITIONAL HSV-1 VECTOR IN 9L GLIOSARCOMA CELLS - IMPLICATIONS FOR THERAPEUTIC GENE IMAGING IN-VIVO
The Journal of nuclear medicine
CLINICAL AND GENETIC-CHARACTERIZATION OF A FAMILY FROM SOUTH TYROL (NORTHERN ITALY) WITH AN UNUSUAL PRESENTATION OF DYSTONIA
Neurology
A GENETIC-STUDY OF 72 PATIENTS WITH IDIOPATHIC FOCAL DYSTONIA FROM NORTHERN GERMANY
Neurology
A DE-NOVO MUTATION (GAG DELETION) IN THE DYT1 GENE IN A PATIENT OF MENNONITE ORIGIN
Neurology
QUANTITATIVE KINETICS OF HSV-1-TK GENE DELIVERY TO TUMOR-CELLS USING A RECOMBINANT HSV-1 VECTOR - IMPLICATIONS FOR IMAGING HSV-1 MEDIATED GENE-TRANSFER IN-VIVO
Neurology
HSV-1 VECTORS ALLOW EFFICIENT TRANSFER OF THE RYR1 CDNA INTO DYSPEDICSKELETAL-MUSCLE CELLS
Biophysical journal
Search for a founder mutation in idiopathic focal dystonia from northern Germany
AMERICAN JOURNAL OF HUMAN GENETICS
SYNERGISTIC ANTICANCER EFFECTS OF GANCICLOVIR THYMIDINE KINASE AND 5-FLUOROCYTOSINE/CYTOSINE DEAMINASE GENE THERAPIES/
Journal of the National Cancer Institute
BENEFITS AND RISKS OF HOSTING ANIMAL-CELLS IN THE HUMAN BRAIN
Nature medicine
GENE-TRANSFER INTO HEPATOCYTES MEDIATED BY HELPER VIRUS-FREE HSV AAV HYBRID VECTORS/
Molecular medicine
THE EARLY-ONSET TORSION DYSTONIA GENE (DYT1) ENCODES AN ATP BINDING-PROTEIN
Nature genetics
FINE LOCALIZATION OF THE TORSION DYSTONIA GENE (DYT1) ON HUMAN-CHROMOSOME 9Q34 - YAC MAP AND LINKAGE DISEQUILIBRIUM
PCR methods and applications
GENE-THERAPY FOR METASTATIC BRAIN-TUMORS BY VACCINATION WITH GRANULOCYTE-MACROPHAGE COLONY-STIMULATING FACTOR-TRANSDUCED TUMOR-CELLS
Human gene therapy
HSV AAV HYBRID AMPLICON VECTORS EXTEND TRANSGENE EXPRESSION IN HUMAN GLIOMA-CELLS/
Human gene therapy
THERAPEUTIC EFFICIENCY AND SAFETY OF A 2ND-GENERATION REPLICATION-CONDITIONAL HSV1 VECTOR FOR BRAIN-TUMOR GENE-THERAPY
Human gene therapy
HYBRID VECTORS - A NEW-GENERATION OF VIRUS-BASED VECTORS DESIGNED TO CONTROL THE CELLULAR FATE OF DELIVERED GENES
Gene therapy
GREEN FLUORESCENT PROTEIN AS A REPORTER FOR RETROVIRUS AND HELPER VIRUS-FREE HSV-1 AMPLICON VECTOR-MEDIATED GENE-TRANSFER INTO NEURAL CELLSIN CULTURE AND IN-VIVO
NeuroReport
VACCINATION FOR EXPERIMENTAL GLIOMAS USING GM-CSF-TRANSDUCED GLIOMA-CELLS
Cancer gene therapy
A CHIMERIC FUSION PROTEIN OF CYTOCHROME CYP4B1 AND GREEN FLUORESCENT PROTEIN FOR DETECTION OF GENE-TRANSFER IN MALIGNANT GLIOMA
Cancer gene therapy
BETA-GALACTOSIDASE GENE-MUTATIONS IN PATIENTS WITH SLOWLY PROGRESSIVEG(M1) GANGLIOSIDOSIS
Journal of child neurology
FUNCTION OF THE EGR-1 T1S8 RADIATION INDUCIBLE PROMOTER IN A MINIMAL HSV-1 AMPLICON SYSTEM/
International journal of radiation oncology, biology, physics
SECONDARY DYSTONIA AND THE DYTI GENE
Neurology
TARGETING TRANSFORMING GROWTH-FACTOR-ALPHA EXPRESSION TO DISCRETE LOCI OF THE NEUROENDOCRINE BRAIN INDUCES FEMALE SEXUAL PRECOCITY
Proceedings of the National Academy of Sciences of the United Statesof America
REGULATED EXPRESSION OF THE DIPHTHERIA-TOXIN-A GENE IN HUMAN GLIOMA-CELLS USING PROKARYOTIC TRANSCRIPTIONAL CONTROL ELEMENTS
Journal of neurosurgery
TUMOR-CELL ENDOCYTOSIS IMAGING FACILITATES DELINEATION OF THE GLIOMA-BRAIN INTERFACE
Experimental neurology
EARLY-ONSET TORSION DYSTONIA GENE (DYT1) ENCODES AN ATP-BINDING PROTEIN
American journal of human genetics
HERPES VECTOR-MEDIATED DELIVERY OF MARKER GENES TO DISSEMINATED CENTRAL-NERVOUS-SYSTEM TUMORS
Human gene therapy
LONG-TERM SURVIVAL IN A RODENT MODEL OF DISSEMINATED BRAIN-TUMORS BY COMBINED INTRATHECAL DELIVERY OF HERPES VECTORS AND GANCICLOVIR TREATMENT
Human gene therapy
A NOVEL PIGGYBACK PACKAGING SYSTEM FOR HERPES-SIMPLEX VIRUS AMPLICON VECTORS
Human gene therapy
CHARACTERIZATION AND MAPPING OF THE MOUSE NDP (NORRIE DISEASE) LOCUS (NDP)
Mammalian genome
RETROVIRUS-MEDIATED GENE-THERAPY OF EXPERIMENTAL BRAIN NEOPLASMS USING THE HERPES-SIMPLEX VIRUUS THYMIDINE KINASE GANCICLOVIR PARADIGM
Cancer gene therapy
HAPLOTYPE ANALYSIS AT THE DYT1 LOCUS IN ASHKENAZI JEWISH PATIENTS WITH OCCUPATIONAL HAND DYSTONIA
Movement disorders
EXCLUSION OF P75(NGFR) AND OTHER CANDIDATE GENES IN A FAMILY WITH HEREDITARY SENSORY NEUROPATHY TYPE-II
Pain
MUTATIONAL ANALYSIS OF THE HUMAN MAOA GENE
American journal of medical genetics
A GENETIC-STUDY OF IDIOPATHIC TORSION DYSTONIA IN ISRAEL
Neurology
SELF-CONTAINED, TETRACYCLINE-REGULATED RETROVIRAL VECTOR SYSTEM FOR GENE DELIVERY TO MAMMALIAN-CELLS
Journal of virology
GENE-THERAPY FOR BRAIN-TUMORS BY CONTROLLED EXPRESSION OF INTERLEUKIN-1-BETA-CONVERTING ENZYME
Journal of neurosurgery
DELIVERY OF HERPESVIRUS AND ADENOVIRUS TO NUDE RAT INTRACEREBRAL TUMORS FOLLOWING OSMOTIC BLOOD-BRAIN-BARRIER DISRUPTION
Journal of neurosurgery
RETROVIRAL DELIVERY AND TETRACYCLINE-DEPENDENT EXPRESSION OF IL-1-BETA-CONVERTING ENZYME (ICE) IN A RAT GLIOMA MODEL PROVIDES CONTROLLED INDUCTION OF APOPTOTIC DEATH IN TUMOR-CELLS
Cancer research
DIFFUSIBLE CYTOTOXIC METABOLITES CONTRIBUTE TO THE IN-VITRO BYSTANDEREFFECT ASSOCIATED WITH THE CYCLOPHOSPHAMIDE CYTOCHROME-P450 2B1 CANCER GENE-THERAPY PARADIGM
Clinical cancer research
MUTATIONS IN THE NORRIE DISEASE GENE
Human mutation
SELECTIVE UPTAKE OF VIRAL AND MONOCRYSTALLINE PARTICLES DELIVERED INTRAARTERIALLY TO EXPERIMENTAL BRAIN NEOPLASMS
Human gene therapy
GENE-THERAPY FOR BRAIN-TUMORS
Brain pathology